NORD and the Galactosemia Foundation Jointly Publish First “Voice of the Patient” Report to Help Inform the FDA and Researchers - National Organization for Rare Disorders
Rutgers University The State University of New Jersey
Stem cell-based therapy for human diseases
History of ALS: decades of scant progress and unmet needs
The future of cystic fibrosis care: a global perspective - The Lancet Respiratory Medicine
SCRIP: Scholarly Research In Progress 2022 by GeisingerCollege - Issuu
FDA advisers to review ALS drug funded by Ice Bucket Challenge
Comorbidities in inflammatory bowel disease: a call for action - The Lancet Gastroenterology & Hepatology
A list of unmet needs with brain volume as identified by the panel